Minister Işıkhan: We are always with our citizens who are struggling with rare diseases

Minister Işık stated in a post on his social media account that they provide support for the treatment processes of citizens with rare diseases, and noted the following:

"We always stand by our citizens who are struggling with rare diseases. The total amount of payments and expenses we made in 2024 to support their treatment processes reached 54.4 billion liras for 313 drugs."

In a statement made by the Ministry of Labor and Social Security, it was noted that spinal muscular atrophy (SMA) disease stands out among the treatments supported by the state, and the contract for the drug, which has been reimbursed since 2017, was renewed last year, thus ensuring that patients do not experience any disruption in accessing treatment.

In addition, it was emphasized that a new oral form of the drug, which stands out with its ease of use, was also included in the reimbursement list, and that this development offers an important alternative treatment option, especially for pediatric patients and their families.

Another innovation that stands out is the treatment method developed for Hemophilia A patients, the statement said, "While patients need to go to the hospital to have vascular access established in traditional treatment, the newly reimbursed drug Hemlibra provides home treatment thanks to its subcutaneous application."